Ultragenyx Issues 2023 Corporate Responsibility Report, Showcasing Commitment to Improving Equity and Access to Innovation in Rare Disease

NOVATO, Calif., April 30, 2024 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) today released its 2023 Corporate Responsibility Report, which showcases the company’s efforts to transform the lives of individuals and families impacted by rare and ultrarare diseases, empower its employees, and make a meaningful impact on the communities it partners with.

“In rare disease, corporate responsibility means pushing for progress and change to support drug development and access for the people and families waiting for proper care,” said Emil Kakkis, M.D., Ph.D., president and chief executive officer of Ultragenyx. “Our 2023 Corporate Responsibility Report highlights the commitment and drive of our team to do the right thing for people living with rare disease while advancing our efforts to contribute meaningfully to the communities where we work and live.”

The company’s Corporate Responsibility program is structured around six key pillars – Innovation, Patients, People, Communities, Planet and Governance – aligned with its vision to lead the future of rare disease medicine and its mission to transform the lives of people with rare disease. The 2023 Ultragenyx Corporate Responsibility Report features updates for all six pillars, as well as Sustainability Accounting Standards Board (SASB) and Global Reporting Initiative (GRI) indices. For the full report and more on Ultragenyx’s Corporate Responsibility efforts, visit https://www.ultragenyx.com/ultra-committed/corporate-responsibility/.

Highlights from Ultragenyx’s 2023 report include:

Innovation:

We are committed to delivering novel, disease-modifying treatments with speed and urgency to rare disease communities with limited or no treatment options.

• Opened a state-of-the-art Gene Therapy Manufacturing Facility (GTMF) in Bedford, Massachusetts
• Advanced six key clinical programs to treat rare and ultrarare diseases, including osteogenesis imperfecta (OI), Angelman syndrome, Wilson disease, Sanfilippo syndrome type A (MPS IIIA), glycogen storage disease type Ia (GSDIa) and ornithine transcarbamylase (OTC) deficiency

Patients:

Ultragenyx is committed to supporting the rare disease community through our efforts to develop novel therapies, share our science and expertise, achieve broad access to screening and treatment, and partner with policymakers for meaningful change.

• More than 4,700 patients have received Ultragenyx treatments through commercial or expanded access in more than 50 countries as of December 2023
• Successfully advocated for the inclusion of more rare diseases in newborn screening (NBS) programs across several U.S. states

People: