AVROBIO Announces Multiple Clinical Data Presentations, Posters and Events at 17th Annual WORLDSymposium 2021 - Seite 2

• Mark Thomas, M.D., principal investigator of the AVROBIO-sponsored Phase 2 clinical trial of AVR-RD-01, an investigational gene therapy for Fabry disease, nephrologist at the Department of Nephrology, Royal Perth Hospital and clinical professor at the University of Western Australia Medical School, will present updates on both the Phase 1 and Phase 2 (FAB-201/FAB-GT) trials of AVR-RD-01 for Fabry disease.

POSTER PRESENTATIONS:

“The Guard1 clinical trial: A first-in-human, open-label, multinational phase 1/2 study of AVR-RD-02 ex vivo lentiviral vector, autologous gene therapy for Gaucher disease,” Thursday, Feb. 11, 2021, between 2:30-3:30 p.m. ET

• Leslie Jacobsen, M.D., vice president, clinical development lead, AVROBIO, will present new data from the AVROBIO-sponsored Phase 1/2 trial of AVR-RD-02, an investigational gene therapy for Gaucher disease type 1.

“Uncovering the burden of Gaucher disease type 1: Patient perspectives on unaddressed symptoms, impact of disease, and the future of treatment,” Thursday, Feb. 11, 2021, between 2:30-3:30 p.m. ET

• Meghan White, patient advocate, Ottawa, Canada and Lori Ann Correia, associate director, patient advocacy and engagement, AVROBIO, will present patient perspectives on the unmet needs of Gaucher disease type 1.

The presentations and posters are available online for WORLD attendees on the conference website.

MEDICAL SYMPOSIA:

“Harnessing the power of ex vivo lentiviral gene therapy: A personalized approach,” symposium, Wednesday, Feb. 10, 2021, from 12:00-1:00 p.m. ET

• Dominique P. Germain, M.D., Ph.D., APHP – University Paris Saclay, France
• Robert J. Hopkin, M.D., Cincinnati Children’s Hospital, U.S.
• Paul J. Orchard, M.D., University of Minnesota, U.S.
• Brian Bigger, Ph.D., University of Manchester, U.K.

“Unmet need in Gaucher disease: Future possibilities with ex vivo lentiviral gene therapy,” symposium, Thursday, Feb. 11, 2021, from 4:00-5:20 p.m. ET

• Timothy M. Cox, M.Sc., M.D., FRCP, MAE, FMedSci, University of Cambridge, U.K.
• Cyndi Frank, Co-Founder and Co-President of Gaucher Community Alliance, U.S.
• Roy Alcalay, M.D., M.S., Columbia University Medical Center, U.S.
• Aneal Khan, M.D., FRCPC, FCCMG, University of Calgary, Canada

WORLD attendees can attend the symposia as part of the regular meeting program online on the conference website.